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Drug Development for Rare Diseases
Hardcover
Series: Chapman & Hall/CRC Biostatistics
Medical ReferenceProbability & Statistics
ISBN13: 9780367518349
Publisher: Crc Pr Inc
Published: Feb 13 2023
Pages: 222
Weight: 1.11
Height: 0.56 Width: 6.14 Depth: 9.21
Language: English
A disease is defined as rare if the prevalence is fewer than 200,000 in the United States. It is estimated that there are more than 7,000 rare diseases, which collectively affect 30 million Americans. This diverse and complex disease area poses challenges for patients, caregivers, regulators, drug developers and other stakeholders.
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